pharmaphorum20h
Myocarditis case mars Sarepta DMD gene therapy readout
New data on Sarepta's gene therapy for Duchenne muscular dystrophy (DMD) has gone a long way towards building confidence in its efficacy – but have introduced a concern about its safety. Updated ...
pharmaphorum20h
Solid Bio hit as FDA slaps clinical hold on DMD gene therapy
The FDA has placed another clinical hold on a gene therapy for Duchenne muscular dystrophy developed by Solid Biosciences, pulverising its share price. The halt of the IGNITE DMD trial was ...