First responders continue to help young girl with rare disease collecting patches to decorate hospital room
ROCKY HILL, Conn. (WFSB) - First responders continue to meet the request for a young girl with a rare disease. Earlier this ...
pharmaphorum3d
Rare Disease R&D: one step forward, but a long road ahead
With over 40% of all medicines in the pipeline aimed at rare diseases, the future looks positive for increasing the number of treatments available. However, as Ben Hargreaves discovers ...
pharmaphorum3d
The biggest challenges facing rare disease pharma – and how the industry can tackle them
As Rare Disease day 2020 approaches, we take a look at the biggest challenges facing orphan drug developers and ask whether the future is bright or bleak for these difficult conditions.
The Lancet2d
Advancing policies for rare diseases in Europe
Fostering dialogue between neurologists, researchers, patient representatives, and policymakers is an important step towards ...
The Lancet2d
The artist and the scientist join forces for rare diseases
Art and science are disciplines that have historically co-existed as polarised entities. However, artists and scientists both ...
MedPage Today on MSN5d
Why CDC's Planned Vaccine-Autism Study Is Raising Eyebrows
Details of the proposed CDC study have not been formally announced, but the Washington Post said the agency plans to analyze ...
Cat diagnosed with rare disease that was once 'death sentence' fighting fit thanks to public donations
Blossom has gone from being 'completely paralysed' to walking up to her owner to greet her thanks to the public donating to ...
‘Novocaine’ With $8M+ Leads Lowest-Grossing Weekend Of 2025 To Date – Sunday Box Office Update
Paramount's Novocaine made $1.75 million in previews and the R-rated action comedy might lead the box office this weekend ...
Reuters6d
Japan's JOGMEC, Iwatani to invest $120 million in French rare earths project
The investment would go through a joint venture, Japan France Rare Earths, they added, but gave no timeframe and declined to comment on the size of their stakes in Caremag. They have also signed a ...
Huge billboard in central London is entirely edible for local wildlife
The four by three metre advertisement has been designed to be gradually nibbled away over a month, providing a boost to the local wildlife.
i6d
The 3.5m people with rare diseases who face worsening treatment and diagnosis rates
Failure to extend the Rare Diseases Framework, set up by the Conservative government in 2021, means patients with any of more than 7,000 rare diseases could be at risk of developing preventable ...